Intelligence ยท Clinical Pipeline
BioMarin Pharmaceutical Australia Pipeline
All ClinicalTrials.gov programs at BioMarin Pharmaceutical Australia โ phase, modality, and trial IDs.
- Programs
- 10
Quick answer
BioMarin Pharmaceutical Australia has 10 clinical development programs indexed from ClinicalTrials.gov, including phase, modality, indication text, and linked NCT identifiers.
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Aldurazyme (Recombinant Human Alpha-L-Iduronidase)
BioMarin Pharmaceutical Australia Pty Ltd
Mucopolysaccharidosis I
3 trials -
BH4
BioMarin Pharmaceutical Australia Pty Ltd
Pku Phenylketonuria
1 trial -
Kuvan
BioMarin Pharmaceutical Australia Pty Ltd
Phenylketonuria (PKU)
2 trials -
Kuvanยฎ
BioMarin Pharmaceutical Australia Pty Ltd
Phenylketonuria
2 trials -
Naglazyme
BioMarin Pharmaceutical Australia Pty Ltd
Mucopolysaccharidosis VI
1 trial -
Pegvaliase
BioMarin Pharmaceutical Australia Pty Ltd
Phenylketonuria
1 trial -
RDD to Palynziq
BioMarin Pharmaceutical Australia Pty Ltd
Phenylketonuria
1 trial -
ROCTAVIAN 2 ร 1013 vector genomes/mL solution for infusion
BioMarin Pharmaceutical Australia Pty Ltd
Hemophilia A
1 trial -
laronidase
BioMarin Pharmaceutical Australia Pty Ltd
Mucopolysaccharidosis I
3 trials -
saproterin dihydrochloride
BioMarin Pharmaceutical Australia Pty Ltd
Phenylketonuria
1 trial
Frequently asked questions
How many pipeline programs does BioMarin Pharmaceutical Australia have?
10 published programs are linked to this sponsor in our ClinicalTrials.gov index.
Is this the complete company pipeline?
This hub lists all published programs for the sponsor in our database. Partnered or out-licensed assets may appear under multiple companies.
Data attribution: Data sources ยท All pipeline programs