Intelligence ยท Clinical Pipeline

BioMarin Pharmaceutical Australia Pipeline

All ClinicalTrials.gov programs at BioMarin Pharmaceutical Australia โ€” phase, modality, and trial IDs.

Programs
10

Quick answer

BioMarin Pharmaceutical Australia has 10 clinical development programs indexed from ClinicalTrials.gov, including phase, modality, indication text, and linked NCT identifiers.

  1. Aldurazyme (Recombinant Human Alpha-L-Iduronidase)

    BioMarin Pharmaceutical Australia Pty Ltd

    Mucopolysaccharidosis I

    approved mab completed

    3 trials
  2. BH4

    BioMarin Pharmaceutical Australia Pty Ltd

    Pku Phenylketonuria

    approved small molecule active

    1 trial
  3. Kuvan

    BioMarin Pharmaceutical Australia Pty Ltd

    Phenylketonuria (PKU)

    approved small molecule completed

    2 trials
  4. Kuvanยฎ

    BioMarin Pharmaceutical Australia Pty Ltd

    Phenylketonuria

    approved small molecule completed

    2 trials
  5. Naglazyme

    BioMarin Pharmaceutical Australia Pty Ltd

    Mucopolysaccharidosis VI

    approved small molecule completed

    1 trial
  6. Pegvaliase

    BioMarin Pharmaceutical Australia Pty Ltd

    Phenylketonuria

    approved mab active

    1 trial
  7. RDD to Palynziq

    BioMarin Pharmaceutical Australia Pty Ltd

    Phenylketonuria

    approved small molecule active

    1 trial
  8. ROCTAVIAN 2 ร— 1013 vector genomes/mL solution for infusion

    BioMarin Pharmaceutical Australia Pty Ltd

    Hemophilia A

    approved small molecule active

    1 trial
  9. laronidase

    BioMarin Pharmaceutical Australia Pty Ltd

    Mucopolysaccharidosis I

    approved small molecule completed

    3 trials
  10. saproterin dihydrochloride

    BioMarin Pharmaceutical Australia Pty Ltd

    Phenylketonuria

    approved small molecule completed

    1 trial

Frequently asked questions

How many pipeline programs does BioMarin Pharmaceutical Australia have?

10 published programs are linked to this sponsor in our ClinicalTrials.gov index.

Is this the complete company pipeline?

This hub lists all published programs for the sponsor in our database. Partnered or out-licensed assets may appear under multiple companies.

Data attribution: Data sources ยท All pipeline programs