Intelligence Β· Clinical Pipeline

BioMarin Pharmaceutical Australia Pipeline

All ClinicalTrials.gov programs at BioMarin Pharmaceutical Australia β€” phase, modality, and trial IDs.

Programs
8

Quick answer

BioMarin Pharmaceutical Australia has 8 clinical development programs indexed from ClinicalTrials.gov, including phase, modality, indication text, and linked NCT identifiers.

  1. BMN 111 administration via Injector Pen

    BioMarin Pharmaceutical Australia Pty Ltd

    Achondroplasia

    phase 1 other terminated

    1 trial
  2. BMN 255

    BioMarin Pharmaceutical Australia Pty Ltd

    Hyperoxaluria

    phase 1 small molecule terminated

    1 trial
  3. BMN 349

    BioMarin Pharmaceutical Australia Pty Ltd

    Alpha 1-Antitrypsin Deficiency

    phase 1 small molecule active

    1 trial
  4. Cisplatin

    BioMarin Pharmaceutical Australia Pty Ltd

    Solid Tumors

    phase 1 small molecule terminated

    1 trial
  5. PARP inhibitor BMN-673

    BioMarin Pharmaceutical Australia Pty Ltd

    Metastatic Cancer

    phase 1 small molecule completed

    1 trial
  6. Talazoparib

    BioMarin Pharmaceutical Australia Pty Ltd

    Childhood Solid Tumors

    phase 1 small molecule completed

    1 trial
  7. Tetrahydrobiopterin 10 mg/kg

    BioMarin Pharmaceutical Australia Pty Ltd

    Claudication, Intermittent

    phase 1 small molecule active

    1 trial
  8. sapropterin dihydrochloride (6R-BH4)

    BioMarin Pharmaceutical Australia Pty Ltd

    Pulmonary Arterial Hypertension

    phase 1 small molecule completed

    1 trial

Frequently asked questions

How many pipeline programs does BioMarin Pharmaceutical Australia have?

8 published programs are linked to this sponsor in our ClinicalTrials.gov index.

Is this the complete company pipeline?

This hub lists all published programs for the sponsor in our database. Partnered or out-licensed assets may appear under multiple companies.

Data attribution: Data sources Β· All pipeline programs