ROCTAVIAN 2 × 1013 vector genomes/mL solution for infusion
270-401 (GENEr8-LTE)
Approved small_molecule active
Quick answer
ROCTAVIAN 2 × 1013 vector genomes/mL solution for infusion for Hemophilia A is a Approved program (small_molecule) at BioMarin International Limited with 1 ClinicalTrials.gov record(s).
Program details
- Company
- BioMarin International Limited
- Indication
- Hemophilia A
- Phase
- Approved
- Modality
- small_molecule
- Status
- active