🇺🇸 FDA
Pipeline program

BH4

Version 1.0, 2018/03/21

Approved small_molecule active

Quick answer

BH4 for Pku Phenylketonuria is a Approved program (small_molecule) at BIOMARIN PHARMACEUTICAL INC with 1 ClinicalTrials.gov record(s).

Program details

Company
BIOMARIN PHARMACEUTICAL INC
Indication
Pku Phenylketonuria
Phase
Approved
Modality
small_molecule
Status
active

Clinical trials