🇺🇸 FDA
Pipeline program

laronidase

ALID02003

Approved small_molecule completed

Quick answer

laronidase for Mucopolysaccharidosis I is a Approved program (small_molecule) at BIOMARIN PHARMACEUTICAL INC with 3 ClinicalTrials.gov record(s).

Program details

Company
BIOMARIN PHARMACEUTICAL INC
Indication
Mucopolysaccharidosis I
Phase
Approved
Modality
small_molecule
Status
completed

Clinical trials