🇺🇸 FDA
Pipeline program

OAV101B, Zolgensma 2 × 10^13 vector genomes/mL solution for infusion

COAV101A12308

Phase 3 small_molecule active

Quick answer

OAV101B, Zolgensma 2 × 10^13 vector genomes/mL solution for infusion for Spinal Muscular Atrophy is a Phase 3 program (small_molecule) at Novartis Ophthalmics Europe with 1 ClinicalTrials.gov record(s).

Program details

Company
Novartis Ophthalmics Europe
Indication
Spinal Muscular Atrophy
Phase
Phase 3
Modality
small_molecule
Status
active

Clinical trials