Wednesday, July 8, 2026

Drug profile · INN

mipomersen sodium

mipomersen sodium (KYNAMRO) is a apo-b 100 mrna antisense inhibitor. Route of administration: subcutaneous. Current US regulatory status: approved.

FDA: approved EMA: refused Cardiovascular system (C10) C10AX11
US status approved
Patents linked 0
Pipeline programs 8
News articles 0
Drug details — mipomersen sodium
US status
approved
Class
Cardiovascular system (C10)
Route
SUBCUTANEOUS
Patents
0
Programs
8
Data quality
0.84

Quick answer

mipomersen sodium (KYNAMRO) is a apo-b 100 mrna antisense inhibitor. Route of administration: subcutaneous. Current US regulatory status: approved.

Key facts

INN mipomersen sodium
Brand KYNAMRO
Mechanism Apo-B 100 mRNA antisense inhibitor
Target Apo-B 100 mRNA
Therapeutic class Cardiovascular system (C10)
Route SUBCUTANEOUS
Formulation SOLUTION
ATC code C10AX11

Mechanism of action

Apo-B 100 mRNA antisense inhibitor

Primary target: Apo-B 100 mRNA

Approval history

Authority Status Date
FDA approved
EMA refused

Pipeline programs

  1. Mipomersen Phase 3 · IONIS PHARMACEUTICALS · Hypercholesterolemia
  2. Mipomersen sodium Phase 3 · IONIS PHARMACEUTICALS · Hypercholesterolemia
  3. mipomersen Phase 3 · IONIS PHARMACEUTICALS · Lipid Metabolism, Inborn Errors
  4. mipomersen sodium Phase 3 · IONIS PHARMACEUTICALS · Heterozygous Familial Hypercholesterolemia
  5. mipomersen sodium Phase 3 · IONIS PHARMACEUTICALS · Lipid Metabolism, Inborn Errors
  6. mipomersen Phase 2 · IONIS PHARMACEUTICALS · Metabolic Diseases
  7. mipomersen Phase 1 · IONIS PHARMACEUTICALS · Healthy Volunteer
  8. mipomersen sodium Phase 1 · IONIS PHARMACEUTICALS · Healthy

Related & competitor drugs

  1. alirocumab Cardiovascular system (C10)
  2. aliskiren Cardiovascular system (C09)
  3. azilsartan medoxomil Cardiovascular system (C09)
  4. bempedoic acid Cardiovascular system (C10)
  5. bosentan Cardiovascular system (C02)
  6. dofetilide Cardiovascular system (C01)

Frequently asked questions

What is mipomersen sodium?

mipomersen sodium (KYNAMRO) is a apo-b 100 mrna antisense inhibitor. Route of administration: subcutaneous. Current US regulatory status: approved.

What is the brand name for mipomersen sodium?

KYNAMRO is a marketed brand name for mipomersen sodium. Check FDA Drugs@FDA for the current US label holder and prescribing information.

What is the US approval status of mipomersen sodium?

mipomersen sodium has approved status in the United States according to our Drugs@FDA-derived records. Verify on the official FDA label before clinical or commercial decisions.