FDA CBER Patient Listening Meeting on Gene Therapy Safety: Patient and Care Partner Perspectives
FDA CBER held a dedicated patient listening meeting focused on two core themes: safety considerations in gene therapy treatment decisions an…
Drug profile · INN
therapy is an FDA-listed pharmaceutical active ingredient.
therapy is an FDA-listed pharmaceutical active ingredient.
| Authority | Status | Date |
|---|---|---|
| NMPA | clinical trials | — |
US 12420113
Methods and apparatus for applying tumor treating fields combined with personalized ultra-fractionated stereotactic adaptive radiotherapy
US 12414983
CD200AR ligands for cancer immunotherapy
US 12404318
Combination HBV therapy
US 12397028
Adoptive cellular therapy
US 12397066
Delivery of gene therapy treatments
US 12384830
Compositions and methods for improving immunotherapy
US 12385010
Gene therapy for recessive dystrophic epidermolysis bullosa using genetically corrected autologous keratinocytes
US 12377093
Pyruvate kinase activators for use in therapy
CN 120418289
Combination therapy of bispecific binding agents that bind to CLDN18.2 and CD3 with immune checkpoint inhibitors
US 12370206
Therapy for inhibition of single-stranded RNA virus replication
US 12364765
Pegylated cystathionine beta synthase for enzyme therapy for treatment of homocystinuria
US 12364774
Nucleic acid molecules and uses thereof for non-viral gene therapy
US 12364775
Viral vectors for cancer therapy
US 12359204
Soluble interleukin-7 receptor (SIL7R) modulating therapy to treat autoimmune diseases and cancer
US 12350318
Combination therapy to treat brain cancer
US 12336976
Glutaminase inhibitor therapy
US 12338459
DNA-chimeric antigen receptor T cells for immunotherapy
US 12338450
Gene therapy constructs for treating Wilson disease
US 12337017
Microbiota transfer therapy for Pitt Hopkins Syndrome
US 12329816
Immunotherapy with metabolic enzyme expression
therapy is an FDA-listed pharmaceutical active ingredient.