🇺🇸 FDA
Pipeline program

Sirolimus 0.5 mg

CT2-02-17

Phase 2 small_molecule active

Quick answer

Sirolimus 0.5 mg for Beta-Thalassemia is a Phase 2 program (small_molecule) at Ultragenyx Pharmaceutical with 2 ClinicalTrials.gov record(s).

Program details

Company
Ultragenyx Pharmaceutical
Indication
Beta-Thalassemia
Phase
Phase 2
Modality
small_molecule
Status
active

Clinical trials