🇺🇸 FDA
Pipeline program

Sialic Acid Extended Release (SA-ER)

UX001-CL201

Phase 2 small_molecule completed

Quick answer

Sialic Acid Extended Release (SA-ER) for GNE Myopathy is a Phase 2 program (small_molecule) at Ultragenyx Pharmaceutical with 1 ClinicalTrials.gov record(s).

Program details

Company
Ultragenyx Pharmaceutical
Indication
GNE Myopathy
Phase
Phase 2
Modality
small_molecule
Status
completed

Clinical trials