🇺🇸 FDA
Pipeline program

LUM001 (Maralixibat)

LUM001-501

Phase 2 small_molecule completed

Quick answer

LUM001 (Maralixibat) for Progressive Familial Intrahepatic Cholestasis (PFIC) is a Phase 2 program (small_molecule) at Mirum Pharmaceuticals with 1 ClinicalTrials.gov record(s).

Program details

Company
Mirum Pharmaceuticals
Indication
Progressive Familial Intrahepatic Cholestasis (PFIC)
Phase
Phase 2
Modality
small_molecule
Status
completed

Clinical trials