Wednesday, July 8, 2026

pharma · Alagille Syndrome · Progressive Familial Intrahepatic Cholestasis (PFIC) · MIRM

Mirum Pharmaceuticals International

Mirum Pharmaceuticals International drug portfolio — 10 indexed compounds with therapeutic class and molecular targets from public FDA and regional approval metadata.

989 E Hillsdale Blvd., Suite 300, Foster City, CA 94404, US HQ
2018 Founded
436 Employees
Public company Type
MIRM · NYSE Ticker
Company details
Status
Public
HQ
989 E Hillsdale Blvd., Suite 300, Foster City, CA 94404, US
Founded
2018
Employees
436
Programs
25
Drugs
10
Patents
4
Intelligence · Drug Pipeline

Mirum Pharmaceuticals International pipeline

Portfolio lens on 10 drugs and development assets — regulatory status, targets, and deep links to NovaPharmaNews drug profiles.

Mirum Pharmaceuticals International drug portfolio — 10 indexed compounds with therapeutic class and molecular targets from public FDA and regional approval metadata.

Drug portfolio

10 compounds
  1. US regulatory status: approved.

  2. Development asset linked to Mirum Pharmaceuticals International in public FDA and regional records.

  3. US regulatory status: approved. Mechanism: Dihydrofolate reductase inhibitor.

    Mechanism
    Dihydrofolate reductase inhibitor
  4. US regulatory status: approved. Molecular target: Bile acid receptor.

    Target
    Bile acid receptor
    Mechanism
    Bile acid receptor FXR agonist
  5. cholic acid

    Alimentary tract and metabolism (A05)

    US regulatory status: approved. Mechanism: Unknown.

    Mechanism
    Unknown
  6. US regulatory status: approved. Molecular target: Estrogen receptor.

    Target
    Estrogen receptor
    Mechanism
    Estrogen receptor alpha agonist
  7. Development asset linked to Mirum Pharmaceuticals International in public FDA and regional records.

  8. maralixibat

    Alimentary tract and metabolism (A05)

    Alimentary tract and metabolism (A05) compound in Mirum Pharmaceuticals International's portfolio. Molecular target: Ileal sodium/bile acid cotransporter.

    Target
    Ileal sodium/bile acid cotransporter
    Mechanism
    Ileal bile acid transporter inhibitor
  9. maralixibat chloride

    Alimentary tract and metabolism (A05)

    US regulatory status: approved. Molecular target: Ileal sodium/bile acid cotransporter.

    Target
    Ileal sodium/bile acid cotransporter
    Mechanism
    Ileal bile acid transporter inhibitor
  10. Development asset linked to Mirum Pharmaceuticals International in public FDA and regional records.