🇺🇸 FDA
Pipeline program

valoctocogene roxaparvovec

BMN 270-201

Phase 2 mab completed

Quick answer

valoctocogene roxaparvovec for Severe Haemophilia A is a Phase 2 program (mab) at BIOMARIN PHARMACEUTICAL INC with 1 ClinicalTrials.gov record(s).

Program details

Company
BIOMARIN PHARMACEUTICAL INC
Indication
Severe Haemophilia A
Phase
Phase 2
Modality
mab
Status
completed

Clinical trials