🇺🇸 FDA
Pipeline program

Valoctocogene roxaparvovec

270-205

Phase 2 mab active

Quick answer

Valoctocogene roxaparvovec for Hemophilia A With Inhibitor is a Phase 2 program (mab) at BIOMARIN PHARMACEUTICAL INC with 1 ClinicalTrials.gov record(s).

Program details

Company
BIOMARIN PHARMACEUTICAL INC
Indication
Hemophilia A With Inhibitor
Phase
Phase 2
Modality
mab
Status
active

Clinical trials