🇺🇸 FDA
Pipeline program

valoctocogene roxaparvovec

270-301

Phase 3 mab active

Quick answer

valoctocogene roxaparvovec for Hemophilia A is a Phase 3 program (mab) at BIOMARIN PHARMACEUTICAL INC with 5 ClinicalTrials.gov record(s).

Program details

Company
BIOMARIN PHARMACEUTICAL INC
Indication
Hemophilia A
Phase
Phase 3
Modality
mab
Status
active

Clinical trials