Friday, July 10, 2026

Intelligence · Clinical pipeline

Rare disease · Phase I

Rare disease programs at Phase I — ClinicalTrials.gov pipeline intelligence.

Programs 2

Quick answer

Rare disease Phase I programs: NovaPharmaNews indexes 2 matching clinical development programs from ClinicalTrials.gov with sponsor, modality, and NCT cross-links.

Top sponsors

Pipeline programs

  1. Dextromethorphan HBr

    Galera Therapeutics

    Healthy

    phase 1 small molecule completed

    1 trial
  2. STRATIFY; Near-infrared fluorescence molecula...

    Disc Medicine

    Crohn's disease, Spondyloarthritis, Rheumatoid arthritis, Ulcerative colitis

    phase 1 other active

    1 trial

Frequently asked questions

How many rare disease Phase I programs exist?

2 programs match both the therapeutic area and stage filters in our published index.