Friday, July 10, 2026

Drug profile · INN

pegunigalsidase alfa

pegunigalsidase alfa (ELFABRIO) is a globotriosylceramide hydrolytic enzyme.

EMA: approved Alimentary tract and metabolism (A16) A16AB20
Patents linked 0
Pipeline programs 3
News articles 0
Drug details — pegunigalsidase alfa
Class
Alimentary tract and metabolism (A16)
Route
Patents
0
Programs
3
Data quality
0.83

Quick answer

pegunigalsidase alfa (ELFABRIO) is a globotriosylceramide hydrolytic enzyme.

Key facts

INN pegunigalsidase alfa
Brand ELFABRIO
Mechanism Globotriosylceramide hydrolytic enzyme
Target Globotriosylceramide
Therapeutic class Alimentary tract and metabolism (A16)
ATC code A16AB20

Mechanism of action

Globotriosylceramide hydrolytic enzyme

Primary target: Globotriosylceramide

Approval history

Authority Status Date
EMA approved

Pipeline programs

  1. CLI-06657AA1-01 Phase 3 · Chiesi Farmaceutici S.p.A · Fabry's disease
  2. PRX-102 (pegunigalsidase alfa) Phase 3 · Protalix Biotherapeutics · Fabry Disease
  3. Pegunigalsidase alfa Phase 3 · Protalix Biotherapeutics · Fabry Disease

Related & competitor drugs

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  3. alogliptin benzoate Alimentary tract and metabolism (A10)
  4. aprepitant Alimentary tract and metabolism (A04)
  5. budesonide Alimentary tract and metabolism (A07)
  6. canagliflozin Alimentary tract and metabolism (A10)

Frequently asked questions

What is pegunigalsidase alfa?

pegunigalsidase alfa (ELFABRIO) is a globotriosylceramide hydrolytic enzyme.

What is the brand name for pegunigalsidase alfa?

ELFABRIO is a marketed brand name for pegunigalsidase alfa. Check FDA Drugs@FDA for the current US label holder and prescribing information.