Wednesday, July 8, 2026

Drug profile · INN

pacritinib citrate

pacritinib citrate (VONJO) is a tyrosine-protein kinase receptor flt3 inhibitor. Route of administration: oral. Current US regulatory status: approved.

FDA: approved
US status approved
Patents linked 0
Pipeline programs 4
News articles 0
Drug details — pacritinib citrate
US status
approved
Class
Route
ORAL
Patents
0
Programs
4
Data quality
0.84

Quick answer

pacritinib citrate (VONJO) is a tyrosine-protein kinase receptor flt3 inhibitor. Route of administration: oral. Current US regulatory status: approved.

Key facts

INN pacritinib citrate
Brand VONJO
Mechanism Tyrosine-protein kinase receptor FLT3 inhibitor
Target Activin receptor type-1
Route ORAL
Formulation CAPSULE

Mechanism of action

Tyrosine-protein kinase receptor FLT3 inhibitor

Primary target: Activin receptor type-1

Approval history

Authority Status Date
FDA approved

Pipeline programs

  1. Pacritinib Phase 3 · Swedish Orphan Biovitrum · Primary Myelofibrosis
  2. Pacritinib Phase 2 · MEDA Pharma GmbH · Patients with myelofibrosis and platelets counts between 50
  3. Pacritinib Phase 2 · Takeda · Primary Myelofibrosis
  4. Pacritinib Phase 2 · Karyopharm Therapeutics · Myelofibrosis

Related & competitor drugs

  1. dibotermin alfa Musculo-skeletal system (M05)
  2. eptotermin alfa Musculo-skeletal system (M05)

Frequently asked questions

What is pacritinib citrate?

pacritinib citrate (VONJO) is a tyrosine-protein kinase receptor flt3 inhibitor. Route of administration: oral. Current US regulatory status: approved.

What is the brand name for pacritinib citrate?

VONJO is a marketed brand name for pacritinib citrate. Check FDA Drugs@FDA for the current US label holder and prescribing information.

What is the US approval status of pacritinib citrate?

pacritinib citrate has approved status in the United States according to our Drugs@FDA-derived records. Verify on the official FDA label before clinical or commercial decisions.