Wednesday, July 8, 2026

Drug profile · INN

inotersen sodium

inotersen sodium (TEGSEDI) is a transthyretin mrna antisense inhibitor. Route of administration: subcutaneous. Current US regulatory status: approved.

FDA: approved
US status approved
Patents linked 1
Pipeline programs 2
News articles 0
Drug details — inotersen sodium
US status
approved
Class
Route
SUBCUTANEOUS
Patents
1
Programs
2
Data quality
0.84

Quick answer

inotersen sodium (TEGSEDI) is a transthyretin mrna antisense inhibitor. Route of administration: subcutaneous. Current US regulatory status: approved.

Key facts

INN inotersen sodium
Brand TEGSEDI
Mechanism Transthyretin mRNA antisense inhibitor
Target Transthyretin mRNA
Route SUBCUTANEOUS
Formulation SOLUTION

Mechanism of action

Transthyretin mRNA antisense inhibitor

Primary target: Transthyretin mRNA

Approval history

Authority Status Date
FDA approved

Pipeline programs

  1. Inotersen Phase 3 · IONIS PHARMACEUTICALS · FAP
  2. Inotersen Phase 3 · IONIS PHARMACEUTICALS · Hereditary Transthyretin-Mediated Amyloid Polyneuropathy

Related & competitor drugs

  1. patisiran Nervous system (N07)
  2. patisiran sodium Transthyretin mRNA RNAi inhibitor
  3. vutrisiran Nervous system (N07)
  4. vutrisiran sodium Transthyretin mRNA rnai inhibitor
  5. eplontersen sodium Transthyretin mRNA antisense inhibitor
  6. eplontersen Nervous system (N07)

Related patents

  1. US 9399774

    Modulation of transthyretin expression

    Expires Mon Jul 21 2036 00:00:00 GMT+0000 (Coordinated Universal Time)

    granted

Frequently asked questions

What is inotersen sodium?

inotersen sodium (TEGSEDI) is a transthyretin mrna antisense inhibitor. Route of administration: subcutaneous. Current US regulatory status: approved.

What is the brand name for inotersen sodium?

TEGSEDI is a marketed brand name for inotersen sodium. Check FDA Drugs@FDA for the current US label holder and prescribing information.

What is the US approval status of inotersen sodium?

inotersen sodium has approved status in the United States according to our Drugs@FDA-derived records. Verify on the official FDA label before clinical or commercial decisions.