Wednesday, July 8, 2026

Drug profile · INN

eplontersen sodium

eplontersen sodium (WAINUA (AUTOINJECTOR)) is a transthyretin mrna antisense inhibitor. Route of administration: subcutaneous. Current US regulatory status: approved.

FDA: approved
US status approved
Patents linked 1
Pipeline programs 3
News articles 0
Drug details — eplontersen sodium
US status
approved
Class
Route
SUBCUTANEOUS
Patents
1
Programs
3
Data quality
0.84

Quick answer

eplontersen sodium (WAINUA (AUTOINJECTOR)) is a transthyretin mrna antisense inhibitor. Route of administration: subcutaneous. Current US regulatory status: approved.

Key facts

INN eplontersen sodium
Brand WAINUA (AUTOINJECTOR)
Mechanism Transthyretin mRNA antisense inhibitor
Target Transthyretin mRNA
Route SUBCUTANEOUS
Formulation SOLUTION

Mechanism of action

Transthyretin mRNA antisense inhibitor

Primary target: Transthyretin mRNA

Approval history

Authority Status Date
FDA approved

Pipeline programs

  1. Eplontersen Phase 3 · IONIS PHARMACEUTICALS · Hereditary Transthyretin-Mediated Amyloid Polyneuropathy
  2. Eplontersen Phase 3 · IONIS PHARMACEUTICALS · Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR CM)
  3. Eplontersen Phase 1 · IONIS PHARMACEUTICALS · Healthy Participants

Related & competitor drugs

  1. patisiran Nervous system (N07)
  2. patisiran sodium Transthyretin mRNA RNAi inhibitor
  3. vutrisiran Nervous system (N07)
  4. vutrisiran sodium Transthyretin mRNA rnai inhibitor
  5. inotersen sodium Transthyretin mRNA antisense inhibitor
  6. eplontersen Nervous system (N07)

Related patents

  1. US 10683499

    Compositions and methods for modulating TTR expression

    Expires Mon Jun 11 2040 00:00:00 GMT+0000 (Coordinated Universal Time)

    granted

Frequently asked questions

What is eplontersen sodium?

eplontersen sodium (WAINUA (AUTOINJECTOR)) is a transthyretin mrna antisense inhibitor. Route of administration: subcutaneous. Current US regulatory status: approved.

What is the brand name for eplontersen sodium?

WAINUA (AUTOINJECTOR) is a marketed brand name for eplontersen sodium. Check FDA Drugs@FDA for the current US label holder and prescribing information.

What is the US approval status of eplontersen sodium?

eplontersen sodium has approved status in the United States according to our Drugs@FDA-derived records. Verify on the official FDA label before clinical or commercial decisions.