CTX001
VX21-CTX001-161
Phase 3 mab active
Quick answer
CTX001 for Beta-Thalassemia is a Phase 3 program (mab) at Vertex Pharmaceuticals (Ireland) Limited with 1 ClinicalTrials.gov record(s).
Program details
- Company
- Vertex Pharmaceuticals (Ireland) Limited
- Indication
- Beta-Thalassemia
- Phase
- Phase 3
- Modality
- mab
- Status
- active