US regulatory status: approved.
pharma Β· Cystic Fibrosis Β· Hepatitis C
Vertex Pharmaceuticals (Australia)
Vertex Pharmaceuticals (Australia) Pty.
Vertex Pharmaceuticals (Australia) drug portfolio β 64 indexed compounds with therapeutic class and molecular targets from public FDA and regional approval metadata.
Company details
- Status
- Public
- HQ
- Vertex Pharmaceuticals Inc., 50 Northern Avenue, Boston, MA 02210, US
- Founded
- 1989
- Employees
- 6,304
- Programs
- 159
- Drugs
- 64
- Patents
- 991
Vertex Pharmaceuticals (Australia) pipeline
Portfolio lens on 64 drugs and development assets β regulatory status, targets, and deep links to NovaPharmaNews drug profiles.
Vertex Pharmaceuticals (Australia) drug portfolio β 64 indexed compounds with therapeutic class and molecular targets from public FDA and regional approval metadata.
Drug portfolio
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US regulatory status: approved. Molecular target: Histamine H1 receptor.
- Target
- Histamine H1 receptor
- Mechanism
- Histamine H1 receptor antagonist
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US regulatory status: approved. Molecular target: Tumor necrosis factor.
- Target
- Tumor necrosis factor
- Mechanism
- TNF-alpha inhibitor
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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US regulatory status: approved.
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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US regulatory status: approved. Molecular target: D(2) dopamine receptor.
- Target
- D(2) dopamine receptor
- Mechanism
- Dopamine D2 receptor antagonist
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US regulatory status: approved. Molecular target: Cyclooxygenase.
- Target
- Cyclooxygenase
- Mechanism
- Cyclooxygenase inhibitor
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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busulfan
Antineoplastic and immunomodulating agents (L01)US regulatory status: approved. Molecular target: DNA.
- Target
- DNA
- Mechanism
- DNA inhibitor
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US regulatory status: approved. Mechanism: Dihydrofolate reductase inhibitor.
- Mechanism
- Dihydrofolate reductase inhibitor
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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US regulatory status: approved. Mechanism: Unknown.
- Mechanism
- Unknown
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
-
Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
-
US regulatory status: approved. Molecular target: Cystic fibrosis transmembrane conductance regulator.
- Target
- Cystic fibrosis transmembrane conductance regulator
- Mechanism
- Cystic fibrosis transmembrane conductance regulator activator
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deutivacaftor / tezacaftor / vanzacaftor
Respiratory system (R07)Respiratory system (R07) compound in Vertex Pharmaceuticals (Australia)'s portfolio.
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doxorubicin
Antineoplastic and immunomodulating agents (L01)Antineoplastic and immunomodulating agents (L01) compound in Vertex Pharmaceuticals (Australia)'s portfolio. Mechanism: DNA topoisomerase II alpha inhibitor.
- Mechanism
- DNA topoisomerase II alpha inhibitor
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US regulatory status: approved.
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exagamglogene autotemcel
Blood and blood forming organs (B06)Blood and blood forming organs (B06) compound in Vertex Pharmaceuticals (Australia)'s portfolio. Molecular target: BCL11 transcription factor A.
- Target
- BCL11 transcription factor A
- Mechanism
- B-cell lymphoma/leukemia 11A gene editing negative modulator
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filgrastim
Antineoplastic and immunomodulating agents (L03)US regulatory status: approved. Molecular target: Granulocyte colony-stimulating factor receptor.
- Target
- Granulocyte colony-stimulating factor receptor
- Mechanism
- Granulocyte colony stimulating factor receptor agonist
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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influenza vaccine (live attenuated, nasal)
Antiinfectives for systemic use (J07)Antiinfectives for systemic use (J07) compound in Vertex Pharmaceuticals (Australia)'s portfolio.
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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interferon alfa-2a
Antineoplastic and immunomodulating agents (L03)Antineoplastic and immunomodulating agents (L03) compound in Vertex Pharmaceuticals (Australia)'s portfolio. Molecular target: Interferon alpha/beta receptor.
- Target
- Interferon alpha/beta receptor
- Mechanism
- Interferon alpha/beta receptor agonist
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ivacaftor
Respiratory system (R07)US regulatory status: approved. Molecular target: Cystic fibrosis transmembrane conductance regulator.
- Target
- Cystic fibrosis transmembrane conductance regulator
- Mechanism
- Cystic fibrosis transmembrane conductance regulator positive modulator
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lumacaftor
Respiratory system (R07)Respiratory system (R07) compound in Vertex Pharmaceuticals (Australia)'s portfolio. Molecular target: Cystic fibrosis transmembrane conductance regulator.
- Target
- Cystic fibrosis transmembrane conductance regulator
- Mechanism
- Cystic fibrosis transmembrane conductance regulator stabiliser
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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peginterferon alfa-2a
Antineoplastic and immunomodulating agents (L03)US regulatory status: approved. Molecular target: Interferon alpha/beta receptor.
- Target
- Interferon alpha/beta receptor
- Mechanism
- Interferon alpha/beta receptor agonist
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US regulatory status: approved. Molecular target: Copper.
- Target
- Copper
- Mechanism
- Copper chelating agent
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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plerixafor
Antineoplastic and immunomodulating agents (L03)US regulatory status: approved. Molecular target: C-X-C chemokine receptor type 4.
- Target
- C-X-C chemokine receptor type 4
- Mechanism
- C-X-C chemokine receptor type 4 partial agonist
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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US regulatory status: approved. Molecular target: Glucocorticoid receptor.
- Target
- Glucocorticoid receptor
- Mechanism
- Glucocorticoid receptor agonist
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pregabalin
Nervous system (N02)US regulatory status: approved. Molecular target: Voltage-gated calcium channel.
- Target
- Voltage-gated calcium channel
- Mechanism
- Voltage-gated calcium channel modulator
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ribavirin
Antiinfectives for systemic use (J05)US regulatory status: approved. Molecular target: Inosine-5'-monophosphate dehydrogenase 1.
- Target
- Inosine-5'-monophosphate dehydrogenase 1
- Mechanism
- Inosine-5'-monophosphate dehydrogenase 1 inhibitor
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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US regulatory status: approved.
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sofosbuvir
Antiinfectives for systemic use (J05)US regulatory status: approved. Molecular target: RNA-directed RNA polymerase.
- Target
- RNA-directed RNA polymerase
- Mechanism
- RNA-directed RNA polymerase inhibitor
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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US regulatory status: approved.
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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tacrolimus
Dermatologicals (D11)US regulatory status: approved. Molecular target: Peptidyl-prolyl cis-trans isomerase FKBP1A.
- Target
- Peptidyl-prolyl cis-trans isomerase FKBP1A
- Mechanism
- FK506-binding protein 1A inhibitor
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US regulatory status: approved. Mechanism: Diagnostic agent.
- Mechanism
- Diagnostic agent
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telaprevir
Antiinfectives for systemic use (J05)US regulatory status: approved. Molecular target: Hepatitis C virus serine protease, NS3/NS4A.
- Target
- Hepatitis C virus serine protease, NS3/NS4A
- Mechanism
- Hepatitis C virus serine protease, NS3/NS4A inhibitor
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tezacaftor
Respiratory system (R07)Respiratory system (R07) compound in Vertex Pharmaceuticals (Australia)'s portfolio. Molecular target: Cystic fibrosis transmembrane conductance regulator.
- Target
- Cystic fibrosis transmembrane conductance regulator
- Mechanism
- Cystic fibrosis transmembrane conductance regulator positive modulator
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.
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Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.