Wednesday, June 10, 2026

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Vertex Pharmaceuticals (Australia)

Vertex Pharmaceuticals (Australia) drug portfolio β€” 64 indexed compounds with therapeutic class and molecular targets from public FDA and regional approval metadata.

Vertex Pharmaceuticals Inc., 50 Northern Avenue, Boston, MA 02210, US HQ
1989 Founded
6,304 Employees
TGA registrant Type
Company details
Status
Public
HQ
Vertex Pharmaceuticals Inc., 50 Northern Avenue, Boston, MA 02210, US
Founded
1989
Employees
6,304
Programs
159
Drugs
64
Patents
991
Intelligence Β· Drug Pipeline

Vertex Pharmaceuticals (Australia) pipeline

Portfolio lens on 64 drugs and development assets β€” regulatory status, targets, and deep links to NovaPharmaNews drug profiles.

Vertex Pharmaceuticals (Australia) drug portfolio β€” 64 indexed compounds with therapeutic class and molecular targets from public FDA and regional approval metadata.

Drug portfolio

64 compounds
  1. US regulatory status: approved. Molecular target: Histamine H1 receptor.

    Target
    Histamine H1 receptor
    Mechanism
    Histamine H1 receptor antagonist
  2. US regulatory status: approved. Molecular target: Tumor necrosis factor.

    Target
    Tumor necrosis factor
    Mechanism
    TNF-alpha inhibitor
  3. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  4. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  5. US regulatory status: approved. Molecular target: D(2) dopamine receptor.

    Target
    D(2) dopamine receptor
    Mechanism
    Dopamine D2 receptor antagonist
  6. US regulatory status: approved. Molecular target: Cyclooxygenase.

    Target
    Cyclooxygenase
    Mechanism
    Cyclooxygenase inhibitor
  7. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  8. busulfan

    Antineoplastic and immunomodulating agents (L01)

    US regulatory status: approved. Molecular target: DNA.

    Target
    DNA
    Mechanism
    DNA inhibitor
  9. US regulatory status: approved. Mechanism: Dihydrofolate reductase inhibitor.

    Mechanism
    Dihydrofolate reductase inhibitor
  10. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  11. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  12. US regulatory status: approved. Mechanism: Unknown.

    Mechanism
    Unknown
  13. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  14. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  15. US regulatory status: approved. Molecular target: Cystic fibrosis transmembrane conductance regulator.

    Target
    Cystic fibrosis transmembrane conductance regulator
    Mechanism
    Cystic fibrosis transmembrane conductance regulator activator
  16. doxorubicin

    Antineoplastic and immunomodulating agents (L01)

    Antineoplastic and immunomodulating agents (L01) compound in Vertex Pharmaceuticals (Australia)'s portfolio. Mechanism: DNA topoisomerase II alpha inhibitor.

    Mechanism
    DNA topoisomerase II alpha inhibitor
  17. exagamglogene autotemcel

    Blood and blood forming organs (B06)

    Blood and blood forming organs (B06) compound in Vertex Pharmaceuticals (Australia)'s portfolio. Molecular target: BCL11 transcription factor A.

    Target
    BCL11 transcription factor A
    Mechanism
    B-cell lymphoma/leukemia 11A gene editing negative modulator
  18. filgrastim

    Antineoplastic and immunomodulating agents (L03)

    US regulatory status: approved. Molecular target: Granulocyte colony-stimulating factor receptor.

    Target
    Granulocyte colony-stimulating factor receptor
    Mechanism
    Granulocyte colony stimulating factor receptor agonist
  19. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  20. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  21. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  22. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  23. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  24. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  25. interferon alfa-2a

    Antineoplastic and immunomodulating agents (L03)

    Antineoplastic and immunomodulating agents (L03) compound in Vertex Pharmaceuticals (Australia)'s portfolio. Molecular target: Interferon alpha/beta receptor.

    Target
    Interferon alpha/beta receptor
    Mechanism
    Interferon alpha/beta receptor agonist
  26. ivacaftor

    Respiratory system (R07)

    US regulatory status: approved. Molecular target: Cystic fibrosis transmembrane conductance regulator.

    Target
    Cystic fibrosis transmembrane conductance regulator
    Mechanism
    Cystic fibrosis transmembrane conductance regulator positive modulator
  27. lumacaftor

    Respiratory system (R07)

    Respiratory system (R07) compound in Vertex Pharmaceuticals (Australia)'s portfolio. Molecular target: Cystic fibrosis transmembrane conductance regulator.

    Target
    Cystic fibrosis transmembrane conductance regulator
    Mechanism
    Cystic fibrosis transmembrane conductance regulator stabiliser
  28. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  29. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  30. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  31. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  32. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  33. peginterferon alfa-2a

    Antineoplastic and immunomodulating agents (L03)

    US regulatory status: approved. Molecular target: Interferon alpha/beta receptor.

    Target
    Interferon alpha/beta receptor
    Mechanism
    Interferon alpha/beta receptor agonist
  34. US regulatory status: approved. Molecular target: Copper.

    Target
    Copper
    Mechanism
    Copper chelating agent
  35. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  36. plerixafor

    Antineoplastic and immunomodulating agents (L03)

    US regulatory status: approved. Molecular target: C-X-C chemokine receptor type 4.

    Target
    C-X-C chemokine receptor type 4
    Mechanism
    C-X-C chemokine receptor type 4 partial agonist
  37. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  38. US regulatory status: approved. Molecular target: Glucocorticoid receptor.

    Target
    Glucocorticoid receptor
    Mechanism
    Glucocorticoid receptor agonist
  39. pregabalin

    Nervous system (N02)

    US regulatory status: approved. Molecular target: Voltage-gated calcium channel.

    Target
    Voltage-gated calcium channel
    Mechanism
    Voltage-gated calcium channel modulator
  40. ribavirin

    Antiinfectives for systemic use (J05)

    US regulatory status: approved. Molecular target: Inosine-5'-monophosphate dehydrogenase 1.

    Target
    Inosine-5'-monophosphate dehydrogenase 1
    Mechanism
    Inosine-5'-monophosphate dehydrogenase 1 inhibitor
  41. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  42. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  43. sofosbuvir

    Antiinfectives for systemic use (J05)

    US regulatory status: approved. Molecular target: RNA-directed RNA polymerase.

    Target
    RNA-directed RNA polymerase
    Mechanism
    RNA-directed RNA polymerase inhibitor
  44. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  45. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  46. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  47. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  48. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  49. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  50. tacrolimus

    Dermatologicals (D11)

    US regulatory status: approved. Molecular target: Peptidyl-prolyl cis-trans isomerase FKBP1A.

    Target
    Peptidyl-prolyl cis-trans isomerase FKBP1A
    Mechanism
    FK506-binding protein 1A inhibitor
  51. telaprevir

    Antiinfectives for systemic use (J05)

    US regulatory status: approved. Molecular target: Hepatitis C virus serine protease, NS3/NS4A.

    Target
    Hepatitis C virus serine protease, NS3/NS4A
    Mechanism
    Hepatitis C virus serine protease, NS3/NS4A inhibitor
  52. tezacaftor

    Respiratory system (R07)

    Respiratory system (R07) compound in Vertex Pharmaceuticals (Australia)'s portfolio. Molecular target: Cystic fibrosis transmembrane conductance regulator.

    Target
    Cystic fibrosis transmembrane conductance regulator
    Mechanism
    Cystic fibrosis transmembrane conductance regulator positive modulator
  53. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  54. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.

  55. Development asset linked to Vertex Pharmaceuticals (Australia) in public FDA and regional records.