🇺🇸 FDA
Pipeline program

PLERIXAFOR, Casgevy 4 - 13 x 10^6 cells/mL dispersion for infusion, BUSULFAN

CTX001-121

Phase 2 small_molecule active

Quick answer

PLERIXAFOR, Casgevy 4 - 13 x 10^6 cells/mL dispersion for infusion, BUSULFAN for Severe sickle cell disease (SCD) is a Phase 2 program (small_molecule) at Vertex Pharmaceuticals (Ireland) Limited with 1 ClinicalTrials.gov record(s).

Program details

Company
Vertex Pharmaceuticals (Ireland) Limited
Indication
Severe sickle cell disease (SCD)
Phase
Phase 2
Modality
small_molecule
Status
active

Clinical trials