Friday, July 10, 2026

biotech · Huntington’s Disease · Amyotrophic Lateral Sclerosis (ALS)

iQure Pharma

uniQure biopharma is a biotech organization headquartered in EU. Primary therapeutic focus areas include Huntington’s Disease, Amyotrophic Lateral Sclerosis (ALS). NovaPharmaNews links 2 clinical program(s), 0 drug profi

Princeton, USA HQ
2019 Founded
9 Employees
EMA registrant Type
Company details
Status
Public
HQ
Princeton, USA
Founded
2019
Employees
9
Programs
2
Drugs
2
Patents
0

Quick answer

uniQure biopharma is a biotech organization headquartered in EU. Primary therapeutic focus areas include Huntington’s Disease, Amyotrophic Lateral Sclerosis (ALS). NovaPharmaNews links 2 clinical program(s), 0 drug profile(s), and 0 patent record(s) to this entity from public FDA, EMA, ClinicalTrials.gov, and USPTO sources. Pipeline phase mix: phase 2 (2).

Company snapshot

iQure is a clinical-stage biotech company advancing a new therapeutic approach for CNS disorders by restoring glutamate homeostasis. Our science targets one of the core functions of astrocytes: the regulation of glutamate uptake, essential for maintaining synaptic balance and protecting neurons from overstimulation. By enhancing the function of the main transporter involved in this process, we bre

  • 2 active pipeline program(s) linked via ClinicalTrials.gov.
  • 2 trial update(s) in the last 12 months.

Public regulatory, clinical, patent, and corporate records for iQure Pharma. Not investment advice.

Lead pipeline drugs

Active clinical programs

Momentum

Proprietary activity score for iQure Pharma.

0 /100 +0 vs 30 days ago

Signal breakdown

  • Clinical trials 0 30d
  • Nova articles 0 30d
  • Patents filed 0 30d
  • FDA actions 0 30d
  • SEC filings 0 30d
  • Conference presentations 0 90d
  • Pipeline advances 0 30d

Recent activity

Latest pipeline, patent, and corporate events for iQure Pharma.

  1. Clinical update

    CT-AMT-130-02 — Phase 2

  2. Clinical update

    AMT-162-001 — Phase 2

View all clinical trial activity →

Quick answers

Common questions about this sponsor — for analysts and search.

  • What is iQure Pharma?

    uniQure biopharma is a biotech organization headquartered in EU. Primary therapeutic focus areas include Huntington’s Disease, Amyotrophic Lateral Sclerosis (ALS). NovaPharmaNews links 2 clinical program(s), 0 drug profile(s), and 0 patent record(s) to this entity from public FDA

  • Is iQure Pharma publicly traded?

    iQure Pharma appears in our database through regulatory marketing authorisation or clinical trial sponsor records; a US listed ticker is not shown for this entity.

  • What drugs does iQure Pharma develop or market?

    We link 2 drug profile(s) where iQure Pharma is an originator or marketer in FDA or regional approval metadata. See the drug portfolio table on https://novapharmanews.com/companies/uniqure-biopharma-b-v#company-drugs.

  • What are the latest developments for iQure Pharma?

    In the last 12 months our linked public records show 2 trial program update(s) and 0 US patent grant(s) tied to this profile.

  • What therapeutic areas does iQure Pharma focus on?

    iQure Pharma focuses on Huntington’s Disease, Amyotrophic Lateral Sclerosis (ALS) based on our analysis of their pipeline programs and drug development activities.

Therapeutic focus

Therapeutic area distribution

Pipeline concentration by therapeutic area from linked clinical programs.

Programs by therapeutic area

Others
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