🇺🇸 FDA
Pipeline program

Adjuvant Immunomodulatory (IM) Therapy

LTFU-ABO-102

Phase 3 small_molecule active

Quick answer

Adjuvant Immunomodulatory (IM) Therapy for Mucopolysaccharidosis IIIA is a Phase 3 program (small_molecule) at Ultragenyx Pharmaceutical with 1 ClinicalTrials.gov record(s).

Program details

Company
Ultragenyx Pharmaceutical
Indication
Mucopolysaccharidosis IIIA
Phase
Phase 3
Modality
small_molecule
Status
active

Clinical trials