🇺🇸 FDA
Pipeline program

rhASA

HGT-MLD-071

Phase 2 small_molecule active

Quick answer

rhASA for Late Metachromatic Leukodystrophy (MLD) is a Phase 2 program (small_molecule) at Shire with 1 ClinicalTrials.gov record(s).

Program details

Company
Shire
Indication
Late Metachromatic Leukodystrophy (MLD)
Phase
Phase 2
Modality
small_molecule
Status
active

Clinical trials