Saturday, July 11, 2026

pharma · Duchenne Muscular Dystrophy · Muscular Dystrophy, Duchenne · SRPT

Sarepta Therapeutics

Sarepta Therapeutics is a pharma organization headquartered in Cambridge, USA. It trades on NYSE under ticker SRPT. Primary therapeutic focus areas include Duchenne Muscular Dystrophy, Muscular Dystrophy, Duchenne, Duche

215 First Street, Cambridge, MA 02142, US HQ
1,150 Employees
Public company Type
SRPT · NYSE Ticker
Company details
Status
Public
HQ
215 First Street, Cambridge, MA 02142, US
Employees
1,150
Programs
46
Drugs
23
Patents
102
Clinical program

SRP-9003

Phase 2 · gene therapy · Limb-Girdle Muscular Dystrophy, Type 2E

SRP-9003 for Limb-Girdle Muscular Dystrophy, Type 2E is a Phase 2 program (gene_therapy) at Sarepta Therapeutics with 1 ClinicalTrials.gov record(s).

← All Sarepta Therapeutics projects Phase 2 gene therapy terminated

Internal code SRP-9003-101

Full intelligence profile for this program is being prepared.

At a glance

Sponsor
Sarepta Therapeutics
Phase
Phase 2
Modality
gene_therapy
Indication
Limb-Girdle Muscular Dystrophy, Type 2E
Status
terminated
Trials
1

Clinical trials