US regulatory status: approved.
pharma Β· Duchenne Muscular Dystrophy Β· Muscular Dystrophy, Duchenne Β· SRPT
Sarepta Therapeutics
Sarepta Therapeutics drug portfolio β 23 indexed compounds with therapeutic class and molecular targets from public FDA and regional approval metadata.
Company details
- Status
- Public
- HQ
- 215 First Street, Cambridge, MA 02142, US
- Employees
- 1,150
- Programs
- 46
- Drugs
- 23
- Patents
- 102
Sarepta Therapeutics pipeline
Portfolio lens on 23 drugs and development assets β regulatory status, targets, and deep links to NovaPharmaNews drug profiles.
Sarepta Therapeutics drug portfolio β 23 indexed compounds with therapeutic class and molecular targets from public FDA and regional approval metadata.
Drug portfolio
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US regulatory status: approved. Molecular target: DNA polymerase catalytic subunit.
- Target
- DNA polymerase catalytic subunit
- Mechanism
- Human herpesvirus 1 DNA polymerase inhibitor
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US regulatory status: approved. Molecular target: Dystrophin pre-mRNA.
- Target
- Dystrophin pre-mRNA
- Mechanism
- Dystrophin pre-mRNA positive modulator
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Development asset linked to Sarepta Therapeutics in public FDA and regional records.
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delandistrogene moxeparvovec
Musculo-skeletal system (M09)Musculo-skeletal system (M09) compound in Sarepta Therapeutics's portfolio. Molecular target: Dystrophin.
- Target
- Dystrophin
- Mechanism
- Dystrophin exogenous gene
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US regulatory status: approved. Molecular target: Estrogen receptor.
- Target
- Estrogen receptor
- Mechanism
- Estrogen receptor alpha agonist
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eteplirsen
Musculo-skeletal system (M09)US regulatory status: approved. Molecular target: Dystrophin pre-mRNA.
- Target
- Dystrophin pre-mRNA
- Mechanism
- Dystrophin pre-mRNA positive modulator
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US regulatory status: approved. Molecular target: Dystrophin pre-mRNA.
- Target
- Dystrophin pre-mRNA
- Mechanism
- Dystrophin pre-mRNA positive modulator
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imlifidase
Antineoplastic and immunomodulating agents (L04)Antineoplastic and immunomodulating agents (L04) compound in Sarepta Therapeutics's portfolio. Molecular target: Antibodies.
- Target
- Antibodies
- Mechanism
- Antibodies hydrolytic enzyme
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influenza vaccine (h1n1)v (split virion, inactivated, adjuvanted)
Antiinfectives for systemic use (J07)Antiinfectives for systemic use (J07) compound in Sarepta Therapeutics's portfolio. Mechanism: Biological vaccine - induces immune response.
- Mechanism
- Biological vaccine - induces immune response
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influenza vaccine (live attenuated, nasal)
Antiinfectives for systemic use (J07)Antiinfectives for systemic use (J07) compound in Sarepta Therapeutics's portfolio.
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Development asset linked to Sarepta Therapeutics in public FDA and regional records.
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Development asset linked to Sarepta Therapeutics in public FDA and regional records.
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Development asset linked to Sarepta Therapeutics in public FDA and regional records.
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japanese encephalitis vaccine (inactivated, adsorbed)
Antiinfectives for systemic use (J07)Antiinfectives for systemic use (J07) compound in Sarepta Therapeutics's portfolio. Mechanism: Biological vaccine - induces immune response.
- Mechanism
- Biological vaccine - induces immune response
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Development asset linked to Sarepta Therapeutics in public FDA and regional records.
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Development asset linked to Sarepta Therapeutics in public FDA and regional records.
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US regulatory status: approved. Molecular target: Glucocorticoid receptor.
- Target
- Glucocorticoid receptor
- Mechanism
- Glucocorticoid receptor agonist
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Development asset linked to Sarepta Therapeutics in public FDA and regional records.
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US regulatory status: approved.
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Development asset linked to Sarepta Therapeutics in public FDA and regional records.
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Development asset linked to Sarepta Therapeutics in public FDA and regional records.
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Development asset linked to Sarepta Therapeutics in public FDA and regional records.