Wednesday, June 10, 2026

pharma Β· Duchenne Muscular Dystrophy Β· Muscular Dystrophy, Duchenne Β· SRPT

Sarepta Therapeutics

Sarepta Therapeutics drug portfolio β€” 23 indexed compounds with therapeutic class and molecular targets from public FDA and regional approval metadata.

215 First Street, Cambridge, MA 02142, US HQ
1,150 Employees
Public company Type
SRPT Β· NYSE Ticker
Company details
Status
Public
HQ
215 First Street, Cambridge, MA 02142, US
Employees
1,150
Programs
46
Drugs
23
Patents
102
Intelligence Β· Drug Pipeline

Sarepta Therapeutics pipeline

Portfolio lens on 23 drugs and development assets β€” regulatory status, targets, and deep links to NovaPharmaNews drug profiles.

Sarepta Therapeutics drug portfolio β€” 23 indexed compounds with therapeutic class and molecular targets from public FDA and regional approval metadata.

Drug portfolio

23 compounds
  1. US regulatory status: approved. Molecular target: DNA polymerase catalytic subunit.

    Target
    DNA polymerase catalytic subunit
    Mechanism
    Human herpesvirus 1 DNA polymerase inhibitor
  2. US regulatory status: approved. Molecular target: Dystrophin pre-mRNA.

    Target
    Dystrophin pre-mRNA
    Mechanism
    Dystrophin pre-mRNA positive modulator
  3. Development asset linked to Sarepta Therapeutics in public FDA and regional records.

  4. delandistrogene moxeparvovec

    Musculo-skeletal system (M09)

    Musculo-skeletal system (M09) compound in Sarepta Therapeutics's portfolio. Molecular target: Dystrophin.

    Target
    Dystrophin
    Mechanism
    Dystrophin exogenous gene
  5. US regulatory status: approved. Molecular target: Estrogen receptor.

    Target
    Estrogen receptor
    Mechanism
    Estrogen receptor alpha agonist
  6. eteplirsen

    Musculo-skeletal system (M09)

    US regulatory status: approved. Molecular target: Dystrophin pre-mRNA.

    Target
    Dystrophin pre-mRNA
    Mechanism
    Dystrophin pre-mRNA positive modulator
  7. US regulatory status: approved. Molecular target: Dystrophin pre-mRNA.

    Target
    Dystrophin pre-mRNA
    Mechanism
    Dystrophin pre-mRNA positive modulator
  8. imlifidase

    Antineoplastic and immunomodulating agents (L04)

    Antineoplastic and immunomodulating agents (L04) compound in Sarepta Therapeutics's portfolio. Molecular target: Antibodies.

    Target
    Antibodies
    Mechanism
    Antibodies hydrolytic enzyme
  9. Development asset linked to Sarepta Therapeutics in public FDA and regional records.

  10. Development asset linked to Sarepta Therapeutics in public FDA and regional records.

  11. Development asset linked to Sarepta Therapeutics in public FDA and regional records.

  12. japanese encephalitis vaccine (inactivated, adsorbed)

    Antiinfectives for systemic use (J07)

    Antiinfectives for systemic use (J07) compound in Sarepta Therapeutics's portfolio. Mechanism: Biological vaccine - induces immune response.

    Mechanism
    Biological vaccine - induces immune response
  13. Development asset linked to Sarepta Therapeutics in public FDA and regional records.

  14. Development asset linked to Sarepta Therapeutics in public FDA and regional records.

  15. US regulatory status: approved. Molecular target: Glucocorticoid receptor.

    Target
    Glucocorticoid receptor
    Mechanism
    Glucocorticoid receptor agonist
  16. Development asset linked to Sarepta Therapeutics in public FDA and regional records.

  17. Development asset linked to Sarepta Therapeutics in public FDA and regional records.

  18. Development asset linked to Sarepta Therapeutics in public FDA and regional records.