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Company profile · Sponsor

PTC

PTC THERAPEUTICS, INC.

PTCT · NYSE pharma WARREN, NJ, USA
Pipeline
24
Drugs
1
Patents
8

Quick answer

PTC (PTCT) is a pharma company. headquartered in WARREN, NJ, USA. listed on NYSE. NovaPharmaNews links 24 pipeline programs, 1 drug, and 8 patents to this profile..

Company facts

Ticker PTCT
Exchange NYSE
Company type pharma
Headquarters WARREN, NJ, USA
SEC CIK 0001070081

Pipeline (24)

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  1. Ataluren

    PTC

    Duchenne Muscular Dystrophy

    phase 3 small molecule terminated

    9 trials

  2. Ataluren

    PTC

    Cystic Fibrosis

    phase 3 small molecule completed

    6 trials

  3. Ataluren

    PTC

    Muscular Dystrophy, Duchenne

    phase 3 small molecule terminated

    3 trials

  4. Ataluren (PTC124®)

    PTC

    Cystic Fibrosis

    phase 3 small molecule completed

    1 trial

  5. Deflazacort

    PTC

    Duchenne Muscular Dystrophy

    phase 3 small molecule completed

    3 trials

  6. Deflazacort

    PTC

    Limb-Girdle Muscular Dystrophy

    phase 3 small molecule terminated

    1 trial

  7. PTC299

    PTC

    Pneumonia

    phase 3 small molecule terminated

    1 trial

  8. PTC923

    PTC

    Phenylketonuria

    phase 3 small molecule active

    2 trials

  9. PTC923, Kuvan 100 mg soluble tablets, PTC923

    PTC

    Phenylketonuria

    phase 3 small molecule active

    1 trial

  10. PTC923, PTC923

    PTC

    Metabolic Disorders - Phenylketonuria

    phase 3 small molecule active

    1 trial

  11. Sephience 250 mg oral powder in sachet, Sephience 1 000 mg oral powder in sachet

    PTC

    Phenylketonuria

    phase 3 small molecule active

    1 trial

  12. Sepiapterin

    PTC

    Phenylketonuria

    phase 3 small molecule active

    1 trial

  13. Unesbulin

    PTC

    Leiomyosarcoma

    phase 3 small molecule terminated

    2 trials

  14. Vatiquinone

    PTC

    Friedreich ataxia

    phase 3 small molecule active

    1 trial

  15. Vatiquinone

    PTC

    Friedreich Ataxia

    phase 3 small molecule active

    3 trials

  16. Vatiquinone

    PTC

    Inherited Mitochondrial Disease

    phase 3 small molecule completed

    1 trial

  17. Vatiquinone

    PTC

    Mitochondrial Diseases

    phase 3 small molecule terminated

    1 trial

  18. AAV2-hAADC

    PTC

    Aromatic Amino Acid Decarboxylase Deficiency

    phase 2 small molecule completed

    1 trial

  19. Ataluren

    PTC

    Hemophilia A

    phase 2 small molecule terminated

    1 trial

  20. Ataluren

    PTC

    Aniridia

    phase 2 small molecule terminated

    2 trials

  21. Ataluren

    PTC

    Nonsene Mutation Duchenne Muscular Dystrophy

    phase 2 small molecule completed

    1 trial

  22. Ataluren

    PTC

    Amino Acid Metabolism, Inborn Errors

    phase 2 small molecule terminated

    1 trial

  23. Ataluren + Pembrolizumab

    PTC

    Colorectal Cancer

    phase 2 small molecule active

    1 trial

  24. CNSA-001

    PTC

    Gastroparesis

    phase 2 small molecule completed

    1 trial

Drugs (1)

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  1. sepiapterin

    SEPHIENCE

    ORAL approved

    A16AX28

Patents (8)

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  1. US 12398140

    Substituted pyrrolo [2,3-d]pyrimidines for treating familial dysautonomia

    Expires Mon Aug 21 2045 00:00:00 GMT+0000 (Coordinated Universal Time)

    granted

  2. US 12384797

    Thioeno[3,2-b] pyridin-7-amine compounds for treating familial dysautonomia

    Expires Mon Aug 07 2045 00:00:00 GMT+0000 (Coordinated Universal Time)

    granted

  3. US 12384789

    Compounds for treating Huntington's disease

    Expires Mon Aug 07 2045 00:00:00 GMT+0000 (Coordinated Universal Time)

    granted

  4. US 12281083

    2-substituted amino-naphth (1,2-d) imidazol-5-one compounds of pharmaceutically acceptable salts thereof

    Expires Mon Apr 17 2045 00:00:00 GMT+0000 (Coordinated Universal Time)

    granted

  5. US 12139499

    Heteroaryl compounds for treating Huntington's disease

    Expires Mon Nov 07 2044 00:00:00 GMT+0000 (Coordinated Universal Time)

    granted

  6. US 12103926

    Compounds for treating huntington's disease

    Expires Mon Sep 26 2044 00:00:00 GMT+0000 (Coordinated Universal Time)

    granted

  7. US 12023335

    Method for treating pancreatic cancer

    Expires Mon Jun 27 2044 00:00:00 GMT+0000 (Coordinated Universal Time)

    granted

  8. US 11938101

    Polymorphic forms of (R)-2-hydroxy-2-methyl-4-(2,4,5-trimethyl-3,6-dioxocyclohexa-1,4-dienyl)butanamide

    Expires Mon Mar 21 2044 00:00:00 GMT+0000 (Coordinated Universal Time)

    granted

Frequently asked questions

What is PTC?

PTC (PTCT) is a pharma company. headquartered in WARREN, NJ, USA. listed on NYSE. NovaPharmaNews links 24 pipeline programs, 1 drug, and 8 patents to this profile..

What pipeline programs does PTC sponsor?

We track 24 ClinicalTrials.gov-linked programs for PTC, including Ataluren and 23 more. Open each program for phase, modality, NCT IDs, and indication details.

Where does PTC company data come from?

Profiles combine SEC EDGAR (CIK/ticker), ClinicalTrials.gov sponsor links, FDA drug records, and USPTO patent metadata. See our data sources page. This profile is for professional reference, not investment advice.