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Company profile · Sponsor

BioMarin

BioMarin International Limited

BMRN · NYSE pharma NOVATO, CA, GB
Pipeline
24
Drugs
10
Patents
8

Quick answer

BioMarin (BMRN) is a pharma company. headquartered in NOVATO, CA, GB. listed on NYSE. NovaPharmaNews links 24 pipeline programs, 10 drugs, and 8 patents to this profile..

Company facts

Ticker BMRN
Exchange NYSE
Company type pharma
Headquarters NOVATO, CA, GB
SEC CIK 0001048477

Pipeline (24)

Search pipeline →

  1. Aldurazyme

    BioMarin

    Mucopolysaccharidosis I

    phase 3 mab completed

    1 trial

  2. BMN 110

    BioMarin

    Mucopolysaccharidosis IVA (Morquio A Syndrome)

    phase 3 small molecule completed

    1 trial

  3. BMN 110 - Weekly

    BioMarin

    Mucopolysaccharidosis IV A

    phase 3 small molecule completed

    1 trial

  4. BMN 110 Weekly

    BioMarin

    MPS IV A

    phase 3 small molecule completed

    1 trial

  5. BMN 111

    BioMarin

    Achondroplasia

    phase 3 small molecule active

    6 trials

  6. BMN 165

    BioMarin

    Phenylketonuria

    phase 3 small molecule completed

    1 trial

  7. BMN 333

    BioMarin

    Achondroplasia

    phase 3 small molecule active

    1 trial

  8. BMN 333, Voxzogo 0.56 mg powder and solvent for solution for injection, Voxzogo 1.2 mg powder and solvent for solution for injection, BMN 333

    BioMarin

    Achondroplasia

    phase 3 small molecule active

    1 trial

  9. BMN 701

    BioMarin

    Late-onset Pompe Disease

    phase 3 small molecule terminated

    1 trial

  10. BMN165 20mg/day

    BioMarin

    Phenylketonuria (PKU)

    phase 3 small molecule completed

    1 trial

  11. Drisapersen

    BioMarin

    Muscular Dystrophies

    phase 3 small molecule terminated

    2 trials

  12. INZ-701

    BioMarin

    Ectonucleotide Pyrophosphatase/phosphodiesterase1 Deficiency

    phase 3 small molecule active

    2 trials

  13. Kuvan®

    BioMarin

    Autistic Disorder

    phase 3 small molecule completed

    1 trial

  14. N-acetylgalactosamine 4-sulfatase

    BioMarin

    Mucopolysaccharidosis VI

    phase 3 small molecule completed

    3 trials

  15. Palynziq 2.5 mg solution for injection in pre-filled syringe, Palynziq 20 mg solution for injection in pre-filled syringe, Palynziq 10 mg solution for injection in pre-filled syringe

    BioMarin

    Phenylketonuria (PKU)

    phase 3 small molecule active

    1 trial

  16. Pegvaliase

    BioMarin

    Phenylketonuria (PKU)

    phase 3 small molecule active

    2 trials

  17. Placebo

    BioMarin

    Mucopolysaccharidosis VI

    phase 3 small molecule completed

    1 trial

  18. Sapropterin Dihydrochloride

    BioMarin

    Phenylketonurias

    phase 3 small molecule completed

    3 trials

  19. Sapropterin dihydrochloride

    BioMarin

    Phenylketonuria

    phase 3 small molecule completed

    4 trials

  20. Vosoritide

    BioMarin

    Hypochondroplasia

    phase 3 small molecule active

    3 trials

  21. Voxzogo 0.4 mg powder and solvent for solution for injection, Voxzogo 0.56 mg powder and solvent for solution for injection, Voxzogo 1.2 mg powder and solvent for solution for injection

    BioMarin

    Hypochondroplasia

    phase 3 small molecule active

    1 trial

  22. Voxzogo 1.2 mg powder and solvent for solution for injection, Voxzogo 0.4 mg powder and solvent for solution for injection, Voxzogo 0.56 mg powder and solvent for solution for injection

    BioMarin

    Achondroplasia

    phase 3 small molecule active

    1 trial

  23. Voxzogo 1.2 mg powder and solvent for solution for injection, powder and solvent for solution for injection, Voxzogo 0.56 mg powder and solvent for solution for injection

    BioMarin

    Hypochondroplasia

    phase 3 small molecule active

    1 trial

  24. rhIDU (recombinant human-Alpha-L-Iduronidase)

    BioMarin

    Mucopolysaccharidosis I

    phase 3 mab completed

    1 trial

Drugs (10)

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  1. cerliponase alfa

    BRINEURA

    INJECTION approved

    A16AB

  2. elosulfase alfa

    VIMIZIM

    INJECTION approved

    A16AB12

  3. galsulfase

    NAGLAZYME

    INJECTION approved

    A16AB

  4. laronidase

    ALDURAZYME

    approved

    A16AB05

  5. pegvaliase

    PALYNZIQ

    A16AB19

  6. pegvaliase-pqpz

    PALYNZIQ

    INJECTION approved

  7. sapropterin

    SAPROPTERIN DIPHARMA

    A16AX07

  8. sapropterin dihydrochloride

    SAPROPTERIN DIHYDROCHLORIDE

    ORAL approved

  9. valoctocogene roxaparvovec

    ROCTAVIAN

    B02BD15

  10. vosoritide

    VOXZOGO

    SUBCUTANEOUS approved

    M05BX

Patents (8)

Search patents →

  1. US 12427171

    Krill oil composition enriched in LPC-DHA and LPC-EPA

    Expires Mon Sep 25 2045 00:00:00 GMT+0000 (Coordinated Universal Time)

    granted

  2. US 12331293

    Bispecific antisense oligonucleotides for dystrophin exon skipping

    Expires Mon Jun 12 2045 00:00:00 GMT+0000 (Coordinated Universal Time)

    granted

  3. US 12239692

    Adeno-associated virus factor VIII vectors

    Expires Mon Feb 27 2045 00:00:00 GMT+0000 (Coordinated Universal Time)

    granted

  4. US 12233106

    C-type natriuretic peptide variants to treat skeletal dysplasia in children

    Expires Mon Feb 20 2045 00:00:00 GMT+0000 (Coordinated Universal Time)

    granted

  5. US 12214015

    Use of c-type natriuretic peptide variants to treat osteoarthritis

    Expires Mon Jan 30 2045 00:00:00 GMT+0000 (Coordinated Universal Time)

    granted

  6. US 12194064

    Process of producing concentrated therapeutic phospholipid composition from krill extracts containing high level of free fatty acids

    Expires Mon Jan 09 2045 00:00:00 GMT+0000 (Coordinated Universal Time)

    granted

  7. US 12188058

    Manufacture of active highly phosphorylated human lysosomal sulfatase enzymes and uses thereof

    Expires Mon Jan 02 2045 00:00:00 GMT+0000 (Coordinated Universal Time)

    granted

  8. US 12076333

    Lysophosphatidylcholine compositions

    Expires Mon Aug 29 2044 00:00:00 GMT+0000 (Coordinated Universal Time)

    granted

Frequently asked questions

What is BioMarin?

BioMarin (BMRN) is a pharma company. headquartered in NOVATO, CA, GB. listed on NYSE. NovaPharmaNews links 24 pipeline programs, 10 drugs, and 8 patents to this profile..

What pipeline programs does BioMarin sponsor?

We track 24 ClinicalTrials.gov-linked programs for BioMarin, including Aldurazyme and 23 more. Open each program for phase, modality, NCT IDs, and indication details.

Where does BioMarin company data come from?

Profiles combine SEC EDGAR (CIK/ticker), ClinicalTrials.gov sponsor links, FDA drug records, and USPTO patent metadata. See our data sources page. This profile is for professional reference, not investment advice.