🇺🇸 FDA
Pipeline program

Sepiapterin

PTC923-PKU-401

Phase 3 small_molecule active

Quick answer

Sepiapterin for Phenylketonuria is a Phase 3 program (small_molecule) at PTC THERAPEUTICS, INC. with 1 ClinicalTrials.gov record(s).

Program details

Company
PTC THERAPEUTICS, INC.
Indication
Phenylketonuria
Phase
Phase 3
Modality
small_molecule
Status
active

Clinical trials