🇺🇸 FDA
Pipeline program

R7999 matching placebo, REGN7999

R7999-BTHAL-2350

Phase 2 small_molecule active

Quick answer

R7999 matching placebo, REGN7999 for Non-transfusion dependent beta-thalassemia (NTDT), Beta-thalassemia Resultant Iron overload (IOL) is a Phase 2 program (small_molecule) at Lacuna Pharma Pty Ltd with 1 ClinicalTrials.gov record(s).

Program details

Company
Lacuna Pharma Pty Ltd
Indication
Non-transfusion dependent beta-thalassemia (NTDT), Beta-thalassemia Resultant Iron overload (IOL)
Phase
Phase 2
Modality
small_molecule
Status
active

Clinical trials