🇺🇸 FDA
Pipeline program

MITAPIVAT, Placebo for MITAPIVAT, MITAPIVAT, MITAPIVAT, MITAPIVAT

AG348-C-022

Phase 3 small_molecule active

Quick answer

MITAPIVAT, Placebo for MITAPIVAT, MITAPIVAT, MITAPIVAT, MITAPIVAT for Pyruvate Kinase Deficiency is a Phase 3 program (small_molecule) at Pharma Mar S.A. with 1 ClinicalTrials.gov record(s).

Program details

Company
Pharma Mar S.A.
Indication
Pyruvate Kinase Deficiency
Phase
Phase 3
Modality
small_molecule
Status
active

Clinical trials