🇺🇸 FDA
Pipeline program

ARTEGENE

D20180302

Phase 2 small_molecule active

Quick answer

ARTEGENE for Severe Combined Immuno-Deficiency (SCID) caused by biallelic mutations in the Artemis gene (DCLRE1C) is a Phase 2 program (small_molecule) at Pari Pharma GmbH with 1 ClinicalTrials.gov record(s).

Program details

Company
Pari Pharma GmbH
Indication
Severe Combined Immuno-Deficiency (SCID) caused by biallelic mutations in the Artemis gene (DCLRE1C)
Phase
Phase 2
Modality
small_molecule
Status
active

Clinical trials