Friday, July 10, 2026

pharma · Metachromatic Leukodystrophy (MLD) · Mucopolysaccharidosis type I, Hurler Syndrome

ORCHARD THERAPEUTICS

Orchard Therapeutics (Netherlands) is a pharma organization headquartered in EU. Primary therapeutic focus areas include Metachromatic Leukodystrophy (MLD), Mucopolysaccharidosis type I, Hurler Syndrome, Mucopolysacchari

London, GB HQ
12 Employees
EMA registrant Type
Company details
Status
Public
HQ
London, GB
Employees
12
Programs
5
Drugs
12
Patents
0

Quick answer

Orchard Therapeutics (Netherlands) is a pharma organization headquartered in EU. Primary therapeutic focus areas include Metachromatic Leukodystrophy (MLD), Mucopolysaccharidosis type I, Hurler Syndrome, Mucopolysaccharidosis type I Hurler. NovaPharmaNews links 5 clinical program(s), 0 drug profile(s), and 0 patent record(s) to this entity from public FDA, EMA, ClinicalTrials.gov, and USPTO sources. Pipeline phase mix: phase 3 (3), phase 2 (2).

Company snapshot

Orchard Therapeutics (Netherlands) is a pharma organization headquartered in EU. Primary therapeutic focus areas include Metachromatic Leukodystrophy (MLD), Mucopolysaccharidosis type I, Hurler Syndrome, Mucopolysaccharidosis type I Hurler. NovaPharmaNews links 5 clinical program(s), 0 drug profile(s), and 0 patent record(s) to this entity from public FDA, EMA, ClinicalTrials.gov, and USPTO sources. Pipeline phase mix: phase 3 (3), phase 2 (2).

  • 5 active pipeline program(s) linked via ClinicalTrials.gov.
  • 5 trial update(s) in the last 12 months.

Public regulatory, clinical, patent, and corporate records for ORCHARD THERAPEUTICS. Not investment advice.

Lead pipeline drugs

Active clinical programs

Momentum

Proprietary activity score for ORCHARD THERAPEUTICS.

0 /100 +0 vs 30 days ago

Signal breakdown

  • Clinical trials 0 30d
  • Nova articles 0 30d
  • Patents filed 0 30d
  • FDA actions 0 30d
  • SEC filings 0 30d
  • Conference presentations 0 90d
  • Pipeline advances 0 30d

Recent activity

Latest pipeline, patent, and corporate events for ORCHARD THERAPEUTICS.

  1. Clinical update

    OTL-203-02 — Phase 3

  2. Clinical update

    TigetT10_MPSIH — Phase 2

  3. Clinical update

    Libmeldy 2-10 x 10^6 cells/mL dispersion for infusion — Phase 3

  4. Clinical update

    Libmeldy 2-10 x 10^6 cells/mL dispersion for infusion — Phase 3

  5. Clinical update

    Libmeldy 2-10 x 10^6 cells/mL dispersion for infusion — Phase 2

View all clinical trial activity →

Quick answers

Common questions about this sponsor — for analysts and search.

  • What is ORCHARD THERAPEUTICS?

    Orchard Therapeutics (Netherlands) is a pharma organization headquartered in EU. Primary therapeutic focus areas include Metachromatic Leukodystrophy (MLD), Mucopolysaccharidosis type I, Hurler Syndrome, Mucopolysaccharidosis type I Hurler. NovaPharmaNews links 5 clinical program

  • Is ORCHARD THERAPEUTICS publicly traded?

    ORCHARD THERAPEUTICS appears in our database through regulatory marketing authorisation or clinical trial sponsor records; a US listed ticker is not shown for this entity.

  • What drugs does ORCHARD THERAPEUTICS develop or market?

    We link 12 drug profile(s) where ORCHARD THERAPEUTICS is an originator or marketer in FDA or regional approval metadata. See the drug portfolio table on https://novapharmanews.com/companies/orchard-therapeutics-netherlands-b-v#company-drugs.

  • What are the latest developments for ORCHARD THERAPEUTICS?

    In the last 12 months our linked public records show 5 trial program update(s) and 0 US patent grant(s) tied to this profile.

  • What therapeutic areas does ORCHARD THERAPEUTICS focus on?

    ORCHARD THERAPEUTICS focuses on Metachromatic Leukodystrophy (MLD), Mucopolysaccharidosis type I, Hurler Syndrome, Mucopolysaccharidosis type I Hurler based on our analysis of their pipeline programs and drug development activities.

Therapeutic focus

Therapeutic area distribution

Pipeline concentration by therapeutic area from linked clinical programs.

Programs by therapeutic area

Others
12
Neurology
1