Friday, July 10, 2026

pharma · Metachromatic Leukodystrophy (MLD) · Mucopolysaccharidosis type I, Hurler Syndrome

ORCHARD THERAPEUTICS

Orchard Therapeutics (Netherlands) is a pharma organization headquartered in EU. Primary therapeutic focus areas include Metachromatic Leukodystrophy (MLD), Mucopolysaccharidosis type I, Hurler Syndrome, Mucopolysacchari

London, GB HQ
12 Employees
EMA registrant Type
Company details
Status
Public
HQ
London, GB
Employees
12
Programs
5
Drugs
12
Patents
0
Clinical program

Libmeldy 2-10 x 10^6 cells/mL dispersion for infusion

Phase 2 · small molecule · Metachromatic Leukodystrophy (MLD)

Libmeldy 2-10 x 10^6 cells/mL dispersion for infusion for Metachromatic Leukodystrophy (MLD) is a Phase 2 program (small_molecule) at Orchard Therapeutics (Netherlands) B.V. with 1 ClinicalTrials.gov record(s).

Internal code 201222

Full intelligence profile for this program is being prepared.

At a glance

Sponsor
Orchard Therapeutics (Netherlands) B.V.
Phase
Phase 2
Modality
small_molecule
Indication
Metachromatic Leukodystrophy (MLD)
Status
active
Trials
1