🇺🇸 FDA
Pipeline program

LENOGRASTIM , RITUXIMAB, BUSULFAN , FLUDARABINE , PLERIXAFOR , OTL-203

TigetT10_MPSIH

Phase 2 small_molecule active

Quick answer

LENOGRASTIM , RITUXIMAB, BUSULFAN , FLUDARABINE , PLERIXAFOR , OTL-203 for Mucopolysaccharidosis type I Hurler is a Phase 2 program (small_molecule) at Orchard Therapeutics (Netherlands) B.V. with 1 ClinicalTrials.gov record(s).

Program details

Company
Orchard Therapeutics (Netherlands) B.V.
Indication
Mucopolysaccharidosis type I Hurler
Phase
Phase 2
Modality
small_molecule
Status
active

Clinical trials