Wednesday, June 10, 2026

pharma · Phenylketonuria · Achondroplasia

BioMarin Pharmaceutical Australia

BioMarin Pharmaceutical Australia is a pharma organization headquartered in San Rafael, USA. Primary therapeutic focus areas include Phenylketonuria, Achondroplasia, Duchenne Muscular Dystrophy, Phenylketonuria (PKU), Hy

770 Lindaro Street, San Rafael, CA 94901, US HQ
1997 Founded
3,171 Employees
TGA registrant Type
Company details
Status
Public
HQ
770 Lindaro Street, San Rafael, CA 94901, US
Founded
1997
Employees
3,171
Programs
91
Drugs
36
Patents
175

Quick answer

BioMarin Pharmaceutical Australia is a pharma organization headquartered in San Rafael, USA. Primary therapeutic focus areas include Phenylketonuria, Achondroplasia, Duchenne Muscular Dystrophy, Phenylketonuria (PKU), Hypochondroplasia. NovaPharmaNews links 91 clinical program(s), 10 drug profile(s), and 175 patent record(s) to this entity from public FDA, EMA, ClinicalTrials.gov, and USPTO sources. Pipeline phase mix: phase 2 (41), phase 3 (27), approved (10).

Company snapshot

BioMarin Pharmaceutical Australia maintains 91 tracked programs across Phenylketonuria, Achondroplasia, Duchenne Muscular Dystrophy, Phenylketonuria (PKU), Hypochondroplasia, Mucopolysaccharidosis I, Mucopolysaccharidosis VI, Hemophilia A, MPS IV A, Jansky-Bielschowsky Disease, Autistic Disorder, Phenylketonurias. Momentum score: 35/100 (30-day delta: n/a). Public registry data covers pipeline pha

  • 15 approved product(s) across US/EU regulatory metadata.
  • 91 active pipeline program(s) linked via ClinicalTrials.gov.
  • 175 US patent(s) indexed to this assignee profile.

Public regulatory, clinical, patent, and corporate records for BioMarin Pharmaceutical Australia. Not investment advice.

Catalysts

Upcoming readouts, regulatory dates, and congress activity.

  • trial_data

    BioMarin's Strategic Move: Voxzogo Label Expansion Insights

  • approval

    BioMarin's SWOT Analysis: Competitive Headwinds in Rare Disease Biotech

  • approval

    BioMarin Seeks Approval for Voxzogo in Short Stature Indication

  • approval

    BioMarin's SWOT Analysis: Competitive Challenges Ahead

  • approval

    This Week’s Biopharma News: New Approvals, Appeals, and AI

  • approval

    BioMarin Rare Disease Therapy Fails Phase 3: Key Takeaways for Pharma Teams

Recent coverage

Lead pipeline drugs

Active clinical programs

Momentum

Proprietary activity score for BioMarin Pharmaceutical Australia.

2 active signals

35 /100 +0 vs 30 days ago

Signal breakdown

  • Clinical trials 113 30d
  • Nova articles 10 30d
  • Patents filed 0 30d
  • FDA actions 0 30d
  • SEC filings 0 30d
  • Conference presentations 0 90d
  • Pipeline advances 0 30d

Competitor landscape

Therapeutic-area overlap peers from registry and pipeline signals.

Recent activity

Latest pipeline, patent, and corporate events for BioMarin Pharmaceutical Australia.

  1. Clinical update

    111-208 — Phase 2

  2. Clinical update

    111-302 — Phase 3

  3. Clinical update

    333-301 — Phase 3

  4. Clinical update

    165-306 — Phase 3

  5. Clinical update

    111-308 — Phase 3

View all clinical trial activity →

Quick answers

Common questions about this sponsor — for analysts and search.

  • What is BioMarin Pharmaceutical Australia?

    BioMarin Pharmaceutical Australia is a pharma organization headquartered in San Rafael, USA. Primary therapeutic focus areas include Phenylketonuria, Achondroplasia, Duchenne Muscular Dystrophy, Phenylketonuria (PKU), Hypochondroplasia. NovaPharmaNews links 91 clinical program(s)

  • Is BioMarin Pharmaceutical Australia publicly traded?

    BioMarin Pharmaceutical Australia appears in our database through regulatory marketing authorisation or clinical trial sponsor records; a US listed ticker is not shown for this entity.

  • What drugs does BioMarin Pharmaceutical Australia develop or market?

    We link 36 drug profile(s) where BioMarin Pharmaceutical Australia is an originator or marketer in FDA or regional approval metadata. See the drug portfolio table on https://novapharmanews.com/companies/biomarin-pharmaceutical-inc#company-drugs.

  • What are the latest developments for BioMarin Pharmaceutical Australia?

    In the last 12 months our linked public records show 91 trial program update(s) and 2 US patent grant(s) tied to this profile.

  • What therapeutic areas does BioMarin Pharmaceutical Australia focus on?

    BioMarin Pharmaceutical Australia focuses on Phenylketonuria, Achondroplasia, Duchenne Muscular Dystrophy based on our analysis of their pipeline programs and drug development activities.

Therapeutic focus

Therapeutic area distribution

Pipeline concentration by therapeutic area from linked clinical programs.

Programs by therapeutic area

Others
104
Cardiology
4
Oncology
4
Neurology
1
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