pharma · Phenylketonuria · Achondroplasia
BioMarin Pharmaceutical Australia
BioMarin Pharmaceutical Australia Pty Ltd
BioMarin Pharmaceutical Australia clinical programs — 27 development programs from ClinicalTrials.gov with phase, modality, indication, and trial identifiers.
Company details
- Status
- Public
- HQ
- 770 Lindaro Street, San Rafael, CA 94901, US
- Founded
- 1997
- Employees
- 3,171
- Programs
- 91
- Drugs
- 36
- Patents
- 175
BioMarin Pharmaceutical Australia projects
27 ClinicalTrials.gov programs sponsored by BioMarin Pharmaceutical Australia.
BioMarin Pharmaceutical Australia has 27 clinical development programs indexed from ClinicalTrials.gov, including phase, modality, indication text, and linked NCT identifiers.
Clinical programs
-
111-302
BioMarin Pharmaceutical Australia Pty Ltd
Achondroplasia
1 trial -
111-303
BioMarin Pharmaceutical Australia Pty Ltd
Hypochondroplasia
1 trial -
111-308
BioMarin Pharmaceutical Australia Pty Ltd
Hypochondroplasia
1 trial -
165-306
BioMarin Pharmaceutical Australia Pty Ltd
Phenylketonuria (PKU)
1 trial -
333-301
BioMarin Pharmaceutical Australia Pty Ltd
Achondroplasia
1 trial -
Aldurazyme
BioMarin Pharmaceutical Australia Pty Ltd
Mucopolysaccharidosis I
1 trial -
BMN 110
BioMarin Pharmaceutical Australia Pty Ltd
Mucopolysaccharidosis IVA (Morquio A Syndrome)
1 trial -
BMN 110 - Weekly
BioMarin Pharmaceutical Australia Pty Ltd
Mucopolysaccharidosis IV A
1 trial -
BMN 110 Weekly
BioMarin Pharmaceutical Australia Pty Ltd
MPS IV A
1 trial -
BMN 111
BioMarin Pharmaceutical Australia Pty Ltd
Achondroplasia
6 trials -
BMN 165
BioMarin Pharmaceutical Australia Pty Ltd
Phenylketonuria
1 trial -
BMN 333
BioMarin Pharmaceutical Australia Pty Ltd
Achondroplasia
1 trial -
BMN 701
BioMarin Pharmaceutical Australia Pty Ltd
Late-onset Pompe Disease
1 trial -
BMN165 20mg/day
BioMarin Pharmaceutical Australia Pty Ltd
Phenylketonuria (PKU)
1 trial -
Drisapersen
BioMarin Pharmaceutical Australia Pty Ltd
Muscular Dystrophies
2 trials -
INZ-701
BioMarin Pharmaceutical Australia Pty Ltd
Ectonucleotide Pyrophosphatase/phosphodiesterase1 Deficiency
2 trials -
Kuvan®
BioMarin Pharmaceutical Australia Pty Ltd
Autistic Disorder
1 trial -
N-acetylgalactosamine 4-sulfatase
BioMarin Pharmaceutical Australia Pty Ltd
Mucopolysaccharidosis VI
3 trials -
PKU-003
BioMarin Pharmaceutical Australia Pty Ltd
Phenylketonurias
1 trial -
Pegvaliase
BioMarin Pharmaceutical Australia Pty Ltd
Phenylketonuria (PKU)
2 trials -
Placebo
BioMarin Pharmaceutical Australia Pty Ltd
Mucopolysaccharidosis VI
1 trial -
Sapropterin Dihydrochloride
BioMarin Pharmaceutical Australia Pty Ltd
Phenylketonurias
3 trials -
Sapropterin dihydrochloride
BioMarin Pharmaceutical Australia Pty Ltd
Phenylketonuria
4 trials -
Vosoritide
BioMarin Pharmaceutical Australia Pty Ltd
Hypochondroplasia
3 trials -
rhIDU (recombinant human-Alpha-L-Iduronidase)
BioMarin Pharmaceutical Australia Pty Ltd
Mucopolysaccharidosis I
1 trial -
sapropterin
BioMarin Pharmaceutical Australia Pty Ltd
Behavioral Manifestations of Lesch-Nyhan Disease
1 trial -
valoctocogene roxaparvovec
BioMarin Pharmaceutical Australia Pty Ltd
Hemophilia A
5 trials
Frequently asked questions
How many clinical projects does BioMarin Pharmaceutical Australia have?
27 published programs are linked to this sponsor in our ClinicalTrials.gov index.
Is this the complete company pipeline?
This directory lists published programs for the sponsor in our database. Partnered or out-licensed assets may appear under multiple companies.