Sapropterin dihydrochloride
PKU-016
Phase 3 small_molecule completed
Quick answer
Sapropterin dihydrochloride for Phenylketonuria is a Phase 3 program (small_molecule) at BioMarin International Limited with 4 ClinicalTrials.gov record(s).
Program details
- Company
- BioMarin International Limited
- Indication
- Phenylketonuria
- Phase
- Phase 3
- Modality
- small_molecule
- Status
- completed