🇺🇸 FDA
Pipeline program

sapropterin

WLN01

Phase 3 small_molecule terminated

Quick answer

sapropterin for Behavioral Manifestations of Lesch-Nyhan Disease is a Phase 3 program (small_molecule) at BioMarin International Limited with 1 ClinicalTrials.gov record(s).

Program details

Company
BioMarin International Limited
Indication
Behavioral Manifestations of Lesch-Nyhan Disease
Phase
Phase 3
Modality
small_molecule
Status
terminated

Clinical trials