Wednesday, June 10, 2026

pharma ยท Phenylketonuria ยท Achondroplasia

BioMarin Pharmaceutical Australia

BioMarin Pharmaceutical Australia clinical programs โ€” 10 development programs from ClinicalTrials.gov with phase, modality, indication, and trial identifiers.

770 Lindaro Street, San Rafael, CA 94901, US HQ
1997 Founded
3,171 Employees
TGA registrant Type
Company details
Intelligence ยท Clinical Programs

BioMarin Pharmaceutical Australia projects

10 ClinicalTrials.gov programs sponsored by BioMarin Pharmaceutical Australia.

BioMarin Pharmaceutical Australia has 10 clinical development programs indexed from ClinicalTrials.gov, including phase, modality, indication text, and linked NCT identifiers.

Clinical programs

  1. Aldurazyme (Recombinant Human Alpha-L-Iduronidase)

    BioMarin Pharmaceutical Australia Pty Ltd

    Mucopolysaccharidosis I

    approved mab completed

    3 trials
  2. BH4

    BioMarin Pharmaceutical Australia Pty Ltd

    Pku Phenylketonuria

    approved small molecule active

    1 trial
  3. Kuvan

    BioMarin Pharmaceutical Australia Pty Ltd

    Phenylketonuria (PKU)

    approved small molecule completed

    2 trials
  4. Kuvanยฎ

    BioMarin Pharmaceutical Australia Pty Ltd

    Phenylketonuria

    approved small molecule completed

    2 trials
  5. Naglazyme

    BioMarin Pharmaceutical Australia Pty Ltd

    Mucopolysaccharidosis VI

    approved small molecule completed

    1 trial
  6. Pegvaliase

    BioMarin Pharmaceutical Australia Pty Ltd

    Phenylketonuria

    approved mab active

    1 trial
  7. RDD to Palynziq

    BioMarin Pharmaceutical Australia Pty Ltd

    Phenylketonuria

    approved small molecule active

    1 trial
  8. ROCTAVIAN 2 ร— 1013 vector genomes/mL solution for infusion

    BioMarin Pharmaceutical Australia Pty Ltd

    Hemophilia A

    approved small molecule active

    1 trial
  9. laronidase

    BioMarin Pharmaceutical Australia Pty Ltd

    Mucopolysaccharidosis I

    approved small molecule completed

    3 trials
  10. saproterin dihydrochloride

    BioMarin Pharmaceutical Australia Pty Ltd

    Phenylketonuria

    approved small molecule completed

    1 trial

Frequently asked questions

How many clinical projects does BioMarin Pharmaceutical Australia have?

10 published programs are linked to this sponsor in our ClinicalTrials.gov index.

Is this the complete company pipeline?

This directory lists published programs for the sponsor in our database. Partnered or out-licensed assets may appear under multiple companies.