🇺🇸 FDA
Pipeline program

Pegvaliase

165-401

Approved mab active

Quick answer

Pegvaliase for Phenylketonuria is a Approved program (mab) at BioMarin International Limited with 1 ClinicalTrials.gov record(s).

Program details

Company
BioMarin International Limited
Indication
Phenylketonuria
Phase
Approved
Modality
mab
Status
active

Clinical trials