pharma · Phenylketonuria · Achondroplasia
BioMarin Pharmaceutical Australia
BioMarin Pharmaceutical Australia Pty Ltd
BioMarin Pharmaceutical Australia is a pharma organization headquartered in San Rafael, USA. Primary therapeutic focus areas include Phenylketonuria, Achondroplasia, Duchenne Muscular Dystrophy, Phenylketonuria (PKU), Hy
770 Lindaro Street, San Rafael, CA 94901, US HQ
1997 Founded
3,171 Employees
TGA registrant Type
Company details
- Status
- Public
- HQ
- 770 Lindaro Street, San Rafael, CA 94901, US
- Founded
- 1997
- Employees
- 3,171
- Programs
- 91
- Drugs
- 36
- Patents
- 175
ROCTAVIAN 2 × 1013 vector genomes/mL solution for infusion
Approved · small molecule · Hemophilia A
ROCTAVIAN 2 × 1013 vector genomes/mL solution for infusion for Hemophilia A is a Approved program (small_molecule) at BioMarin Pharmaceutical Australia Pty Ltd with 1 ClinicalTrials.gov record(s).
Internal code 270-401 (GENEr8-LTE)
Full intelligence profile for this program is being prepared.
At a glance
- Sponsor
- BioMarin Pharmaceutical Australia Pty Ltd
- Phase
- Approved
- Modality
- small_molecule
- Indication
- Hemophilia A
- Status
- active
- Trials
- 1