🇺🇸 FDA
Pipeline program

Vosoritide Injection

111-211

Phase 2 small_molecule active

Quick answer

Vosoritide Injection for Noonan Syndrome is a Phase 2 program (small_molecule) at BIOMARIN PHARMACEUTICAL INC with 1 ClinicalTrials.gov record(s).

Program details

Company
BIOMARIN PHARMACEUTICAL INC
Indication
Noonan Syndrome
Phase
Phase 2
Modality
small_molecule
Status
active

Clinical trials