🇺🇸 FDA
Pipeline program

Sapropterin

HSC-MS-11-0119

Unknown small_molecule terminated

Quick answer

Sapropterin for Hyperphenylalaninemia is a Unknown program (small_molecule) at BIOMARIN PHARMACEUTICAL INC with 1 ClinicalTrials.gov record(s).

Program details

Company
BIOMARIN PHARMACEUTICAL INC
Indication
Hyperphenylalaninemia
Phase
Unknown
Modality
small_molecule
Status
terminated

Clinical trials