🇺🇸 FDA
Pipeline program

Sapropterin

48052

Phase 2 small_molecule completed

Quick answer

Sapropterin for GTP Cyclohydrolase Deficiency is a Phase 2 program (small_molecule) at BIOMARIN PHARMACEUTICAL INC with 1 ClinicalTrials.gov record(s).

Program details

Company
BIOMARIN PHARMACEUTICAL INC
Indication
GTP Cyclohydrolase Deficiency
Phase
Phase 2
Modality
small_molecule
Status
completed

Clinical trials