Sapropterin Dihydrochloride
SCD-001
Phase 2 small_molecule completed
Quick answer
Sapropterin Dihydrochloride for Sickle Cell Disease is a Phase 2 program (small_molecule) at BIOMARIN PHARMACEUTICAL INC with 1 ClinicalTrials.gov record(s).
Program details
- Company
- BIOMARIN PHARMACEUTICAL INC
- Indication
- Sickle Cell Disease
- Phase
- Phase 2
- Modality
- small_molecule
- Status
- completed