🇺🇸 FDA
Pipeline program

Sapropterin dihydrochloride

PKU-016

Phase 3 small_molecule completed

Quick answer

Sapropterin dihydrochloride for Phenylketonuria is a Phase 3 program (small_molecule) at BIOMARIN PHARMACEUTICAL INC with 4 ClinicalTrials.gov record(s).

Program details

Company
BIOMARIN PHARMACEUTICAL INC
Indication
Phenylketonuria
Phase
Phase 3
Modality
small_molecule
Status
completed

Clinical trials