🇺🇸 FDA
Pipeline program

sapropterin dihydrochloride, 6R-BH4, tetrahydrobiopterin

PKU-003

Phase 3 small_molecule completed

Quick answer

sapropterin dihydrochloride, 6R-BH4, tetrahydrobiopterin for Phenylketonurias is a Phase 3 program (small_molecule) at BIOMARIN PHARMACEUTICAL INC with 1 ClinicalTrials.gov record(s).

Program details

Company
BIOMARIN PHARMACEUTICAL INC
Indication
Phenylketonurias
Phase
Phase 3
Modality
small_molecule
Status
completed

Clinical trials